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CRISPR Gene Editing Therapy Success

This is a news story, published by Good News Network, that relates primarily to KJ news.

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severe carbamoyl phosphate synthetase deficiency
Good News Network

Good News Network

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Science

Science

Infant With Incurable Disease is First to Successfully Receive Personalized Gene Therapy Treatment

Good News Network
Summary
Nutrition label

79% Informative

KJ was born with a rare metabolic disease known as severe carbamoyl phosphate synthetase deficiency (CPS1) After spending the first several months of his life in the hospital on a very restrictive diet, KJ received the first dose of his unique therapy in February .

The treatment was safely administered, and he is now growing and thriving.

Researchers knew that finding new ways to treat patients who are too young and small to receive liver transplants would be life-changing for families.

“We’re so excited to be able to finally be together at home, so that KJ can be with his siblings, and we can finally take a deep breath,” said his father, Kyle Muldoon .

VR Score

75

Informative language

71

Neutral language

42

Article tone

semi-formal

Language

English

Language complexity

62

Offensive language

not offensive

Hate speech

not hateful

Attention-grabbing headline

not detected

Known propaganda techniques

not detected

Time-value

medium-lived

External references

6

https://www.addtoany.com/sharehttps://www.nejm.org/doi/full/10.1056/NEJMoa2504747https://www.addtoany.com/add_to/email?linkurl=https%3A%2F%2Fwww.goodnewsnetwork.org%2Finfant-with-incurable-disease-is-first-to-successfully-receive-personalized-gene-therapy-treatment%2F&linkname=Infant%20With%20Incurable%20Disease%20is%20First%20to%20Successfully%20Receive%20Personalized%20Gene%20Therapy%20Treatmenthttps://www.chop.edu/news/worlds-first-patient-treated-personalized-crispr-gene-editing-therapy-childrens-hospitalhttps://www.addtoany.com/add_to/whatsapp?linkurl=https%3A%2F%2Fwww.goodnewsnetwork.org%2Finfant-with-incurable-disease-is-first-to-successfully-receive-personalized-gene-therapy-treatment%2F&linkname=Infant%20With%20Incurable%20Disease%20is%20First%20to%20Successfully%20Receive%20Personalized%20Gene%20Therapy%20Treatmenthttps://www.addtoany.com/add_to/pinterest?linkurl=https%3A%2F%2Fwww.goodnewsnetwork.org%2Finfant-with-incurable-disease-is-first-to-successfully-receive-personalized-gene-therapy-treatment%2F&linkname=Infant%20With%20Incurable%20Disease%20is%20First%20to%20Successfully%20Receive%20Personalized%20Gene%20Therapy%20Treatment

Source diversity

3

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